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261,768 grants matching “gene therapy”
Development of a universal gene therapy for hemophilia A or B with or without inhibitors
$1,266,694Paris Margaritis · Geneventiv Therapeutics, Inc. · R44 · FY2025 · HL
Editing Alveolar Progenitor Cells for Correction of Monogenic Disease
$1,266,687Jeffrey A Whitsett · Cincinnati Childrens Hosp Med Ctr · U01 · FY2020 · HL
SuperGAGs for Intravesicular Treatment of Interstitial Cystitis
$1,266,580Robert Evan Hurst · Glycologix, Llc · R44 · FY2021 · DK
Mechanisms of inherited neurodegenerative diseases
$1,266,452Michael Ward · National Institute Of Neurological Disorders And Stroke · ZIA · FY2019 · NS
Molecular Mechanisms of HIV Latency
$1,266,294Eric M Verdin · Buck Institute For Research On Aging · R01 · FY2019 · DA
Endocannabinoid Active Sites as Therapeutic Targets
$1,266,254Alexandros Makriyannis · Northeastern University · P01 · FY2017 · DA
UNC Cystic Fibrosis Research and Translation Core Center
$1,266,184Martina Gentzsch · Univ Of North Carolina Chapel Hill · P30 · FY2025 · DK
Development of new therapies for neuroblastoma
$1,266,097Hong Ha Rosa Nguyen · Division Of Basic Sciences - Nci · ZIA · FY2023 · CA
Lung Transplant Clinical Trial Network (LT-CTN)
$1,266,035Scott M Palmer · Duke University · U01 · FY2024 · AI
University of Iowa Hawkeye Intellectual and Developmental Disabilities Research Center (Hawk-IDDRC)
$1,265,696Lane Strathearn · University Of Iowa · P50 · FY2025 · HD
Decrypting Variants of Uncertain Significance in Long-QT Syndrome
$1,265,657Alfred L George · Northwestern University At Chicago · R01 · FY2021 · HL
NATIONAL GENE VECTOR LABORATORY AT INDIANA UNIVERSITY
$1,265,524Kenneth G Cornetta · Indiana Univ-Purdue Univ At Indianapolis · U42 · FY2006 · RR
Pig to Non-Human Primate Islet Xenografts
$1,265,491Judith M. Thomas · University Of Alabama At Birmingham · U19 · FY2007 · AI
Signaling in the retina and retinal pigment epithelium
$1,265,401Thomas Redmond · National Eye Institute · ZIA · FY2017 · EY
FilmArray Direct: Rapid Diagnosis of Antimicrobial-Resistant Pathogens from Blood
$1,265,369Andrew Hemmert · Biofire Diagnostics, Llc · R01 · FY2016 · AI
In vivo Pathway Discovery in Autosomal Dominant Polycystic Kidney Disease
$1,265,317Stefan Somlo · Yale University · RC2 · FY2023 · DK
Modeling, pathogenesis and treatment of idiopathic pulmonary fibrosis
$1,265,305Hans-Willem E Snoeck · Columbia University Health Sciences · U01 · FY2020 · HL
NHGRI/DIR Technology Transfer Program
$1,265,189Claire Driscoll · National Human Genome Research Institute · ZIK · FY2016 · HG
MIND Institute Intellectual and Developmental Disabilities Research Center
$1,265,169Leonard J Abbeduto · University Of California At Davis · U54 · FY2015 · HD
Center of Excellence for Health Disparities Research: EI Centro
$1,265,165Victoria B Mitrani · University Of Miami Coral Gables · P60 · FY2016 · MD
Genotoxicity and mitochondrial toxicity of antiretroviral NRTI and PI drugs
$1,265,093Miriam C Poirier · Division Of Basic Sciences - Nci · ZIA · FY2012 · CA
Seven Transmembrane-spanning Receptors: Structure and Function
$1,265,078Marvin Gershengorn · National Institute Of Diabetes And Digestive And Kidney Diseases · ZIA · FY2017 · DK
Cell Production Core Facility
$1,264,987Robert Somerville · Division Of Basic Sciences - Nci · ZIC · FY2018 · CA
Surgery Branch Cell Prep Core
$1,264,987John Wunderlich · Division Of Basic Sciences - Nci · ZIC · FY2018 · CA
Immune modulating therapies to treat complex regional pain syndrome
$1,264,986Seena Ajit · Drexel University · RF1 · FY2025 · NS