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261,768 grants matching “gene therapy”
Nephrotic Syndrome Rare Disease Clinical Research Network
$1,250,000Matthias Kretzler · University Of Michigan At Ann Arbor · U54 · FY2014 · DK
Porphyria Rare Disease Clinical Research Consortium (RDCRC)
$1,250,000Robert J Desnick · Icahn School Of Medicine At Mount Sinai · U54 · FY2014 · DK
Primary Immune Deficiency Treatment Consortium
$1,250,000Morton Cowan · University Of California, San Francisco · U54 · FY2009 · AI
Florida Node of The Drug Abuse Clinical Trials Network
$1,250,000Jose Szapocznik · University Of Miami School Of Medicine · U10 · FY2008 · DA
Clinical and Translational Science Award
$1,250,000Reza Shaker · Medical College Of Wisconsin · UL1 · FY2021 · TR
The Inherited Neuropathy Consortium (INC) RDCRC- Overall
$1,250,000Michael E Shy · University Of Iowa · U54 · FY2015 · NS
The Inherited Neuropathy Consortium (INC) RDCRC- Overall
$1,250,000Michael E Shy · University Of Iowa · U54 · FY2017 · NS
Rett syndrome, MECP2 Duplications, and Rett-related Disorders Natural History
$1,250,000Alan Kenneth Percy · University Of Alabama At Birmingham · U54 · FY2019 · HD
The Frontotemporal Lobar Degeneration Clinical Research Consortium
$1,250,000Adam L Boxer · University Of California, San Francisco · U54 · FY2018 · NS
National Drug Abuse Treatment Clinical Trials Network
$1,250,000Walter Nmn Ling · University Of California Los Angeles · U10 · FY2007 · DA
The Frontotemporal Lobar Degeneration Clinical Research Consortium
$1,250,000Adam L Boxer · University Of California, San Francisco · U54 · FY2017 · NS
Florida Node of The Drug Abuse Clinical Trials Network
$1,250,000Jose Szapocznik · University Of Miami School Of Medicine · U10 · FY2007 · DA
Delaware Valley Node of the Clinical Trials Network
$1,250,000George E Woody · University Of Pennsylvania · U10 · FY2007 · DA
National Drug Abuse Treatment Clinical Trials Network
$1,250,000Walter Nmn Ling · University Of California Los Angeles · U10 · FY2009 · DA
South Carolina Consortium of the Clinical Trials Network
$1,250,000Kathleen Theresa Brady · Medical University Of South Carolina · U10 · FY2009 · DA
Porphyria Rare Disease Clinical Research Consortium (RDCRC)
$1,250,000Robert J Desnick · Icahn School Of Medicine At Mount Sinai · U54 · FY2017 · DK
Genetic Disorder of Mucocilary Clearance
$1,249,998Michael R Knowles · Univ Of North Carolina Chapel Hill · U54 · FY2014 · HL
SBIR Phase II: Development of an Intracellular Delivery Platform for Accelerated Drug Discovery Using Genetically Engineered Human Immune Cells
$1,249,996Marija Tadin-Strapps · Sqz Biotechnologies Company · · FY2016 · TIP
Molecular Pathogenesis of Basal-like Breast Cancer
$1,249,964Richard J Baer · Columbia University Health Sciences · P01 · FY2012 · CA
AD04 disease-modifying drug for Alzheimer's - preclinical and IND-enabling studies
$1,249,957Carmela R Abraham · Advantage Therapeutics, Inc · R44 · FY2025 · AG
Signaling Aberrations and Cerebral Cavernous Malformation Pathogenesis
$1,249,844Douglas A Marchuk · Duke University · P01 · FY2024 · NS
STTR Phase II: Multifunctional Lipid Nanoparticle Delivery System for Targeted Delivery of Vascular RNA Therapeutics
$1,249,673Richard K Fisher · Orion Therapeutics Inc. · · FY2025 · TIP
Therapeutic Targeting of Hypoxic and Oxidative Stress
$1,249,645Robert T Dorr · University Of Arizona · P01 · FY2007 · CA
Nutrition Obesity Research Center at Harvard
$1,249,616W Allan Walker · Massachusetts General Hospital · P30 · FY2014 · DK
Recombinant AAV for Correction of Genetic Abnormalities
$1,249,505Barry J. Byrne · University Of Florida · P01 · FY2007 · DK