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261,768 grants matching “gene therapy”
Development of Recombinant Toxins to Treat Hematologic Malignancies
$1,202,567Robert Kreitman · Division Of Basic Sciences - Nci · ZIA · FY2020 · CA
Research Center for Pharmacology and Drug Toxicology
$1,202,341Vanderbilt University · P50 · FY2002 · GM
Dynamic regulatory network models of human response to influenza virus
$1,202,266Ivan Marazzi · Icahn School Of Medicine At Mount Sinai · U01 · FY2020 · AI
Oral cleft prevention program
$1,202,212Jeffrey C Murray · University Of Iowa · U01 · FY2008 · DE
Structure-Guided Design of Broadly Neutralizing Lassa Virus BiSpecific Antibodies
$1,202,174Luis Manuel Branco · Zalgen Labs, Llc · R01 · FY2021 · AI
Epithelial stem/progenitor cells as repair agents in diffuse alveolar damage
$1,202,147Harold A Chapman · University Of California, San Francisco · U01 · FY2021 · HL
Pathology, Developmental Origins, and Prevention of Pediatric Dysphagia
$1,202,022Sally Ann Moody · George Washington University · P01 · FY2019 · HD
Regulation of RNA biogenesis and function by RNA modifications
$1,202,020Pedro De Oliveira Rodrigues Batista · Division Of Basic Sciences - Nci · ZIA · FY2025 · CA
Mechanism of CD33 receptor signaling in Alzheimer disease
$1,202,012Tobias Sebastian Ulmer · University Of Southern California · RF1 · FY2021 · AG
NHGRI/DIR Genetic Counseling Training Program
$1,201,825Lori Erby · National Human Genome Research Institute · ZIE · FY2022 · HG
Excitotoxicity in Circulatory Arrest-Brain Injury
$1,201,809William Anthony Baumgartner · Johns Hopkins University · R01 · FY2015 · HL
NADPH Oxidases as Novel Targets for Cancer Therapy
$1,201,732James Doroshow · Division Of Basic Sciences - Nci · ZIA · FY2025 · CA
Neuroimmune pathways linking chronic psychosocial stress to co-occurring stimulant use and depression in HIV disease: a mechanistic clinical trial
$1,201,542Christina S Meade · Wake Forest University Health Sciences · R01 · FY2025 · DA
A Microphysiological System for Kidney Disease Modeling and Drug Efficacy Testing
$1,201,539Jonathan Himmelfarb · University Of Washington · UH3 · FY2019 · TR
Developing a microfluidic human neurovascular unit system to investigate genetic and age-related risk factors in Alzheimer's disease
$1,201,492Andrew Alexander Sproul · Columbia University Health Sciences · RF1 · FY2022 · AG
A Clinical Trial of AAV2-BDNF Gene Therapy in Alzheimer's Disease
$1,201,473Mark H Tuszynski · University Of California, San Diego · R01 · FY2021 · AG
Modifiers of elastin arteriopathy
$1,201,470Beth Kozel · National Heart, Lung, And Blood Institute · ZIA · FY2018 · HL
Immunologic Mechanisms of Alcoholic Liver Disease
$1,201,402Bin Gao · National Institute On Alcohol Abuse And Alcoholism · ZIA · FY2014 · AA
Office of Translational Resources
$1,201,329James L. Gulley · Division Of Basic Sciences - Nci · ZIC · FY2025 · CA
NADPH Oxidases as Novel Targets for Cancer Therapy
$1,201,276James Doroshow · Division Of Basic Sciences - Nci · ZIA · FY2024 · CA
BIOCHEMICAL MARKERS IN THE NURSES'HEALTH STUDY COHORT
$1,201,205Brigham And Women'S Hospital · R01 · FY2003 · CA
Basic and Translational Research iPSC-based hematologic and vascular therapies
$1,201,065John P Cooke · Stanford University · U01 · FY2009 · HL
Oral Delivery Vehicles for RNAi Therapies
$1,200,783Michael P Czech · Univ Of Massachusetts Med Sch Worcester · R01 · FY2010 · DK
Pathways that Suppress or Accelerate Premalignant Progression of Squamous Cancer
$1,200,776Stuart H. Yuspa · Division Of Basic Sciences - Nci · ZIA · FY2020 · CA
Immuno/Immunogene Therapies for Thoracic Malignancies
$1,200,734Steven Mark Albelda · University Of Pennsylvania · P01 · FY2008 · CA