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261,768 grants matching “gene therapy”
Preventing cognitive impairment in mouse genetic models of Down syndrome by early postnatal suppression of Kir3.2 channel signaling
$1,183,750Alexander M Kleschevnikov · University Of California, San Diego · R01 · FY2020 · HD
Molecular approaches to understand vector-host and vector-pathogen interactions
$1,183,518Jesus Valenzuela · National Institute Of Allergy And Infectious Diseases · ZIA · FY2014 · AI
Clinical Trial Readiness for SCA1 and SCA3
$1,183,360Tetsuo Ashizawa · Methodist Hospital Research Institute · U01 · FY2019 · NS
Molecular Mechanisms Of The Autoimmune Lymphoproliferative Syndrome And Other Immunoregulatory Disorders
$1,183,045Michael J Lenardo · National Institute Of Allergy And Infectious Diseases · ZIA · FY2022 · AI
Uncovering molecular effectors of mammalian aging
$1,183,000Amy Jo Wagers · Harvard University · DP1 · FY2018 · AG
Uncovering molecular effectors of mammalian aging
$1,183,000Amy Jo Wagers · Harvard University · DP1 · FY2022 · AG
Novel therapeutic gene editing to induce fetal hemoglobin for sickle cell disease
$1,183,000Mitchell J Weiss · St. Jude Children'S Research Hospital · U01 · FY2023 · HL
Uncovering molecular effectors of mammalian aging
$1,183,000Amy Jo Wagers · Harvard University · DP1 · FY2019 · AG
Novel therapeutic gene editing to induce fetal hemoglobin for sickle cell disease
$1,183,000Mitchell J Weiss · St. Jude Children'S Research Hospital · U01 · FY2025 · HL
Uncovering molecular effectors of mammalian aging
$1,183,000Amy Jo Wagers · Harvard University · DP1 · FY2021 · AG
Uncovering molecular effectors of mammalian aging
$1,183,000Amy Jo Wagers · Harvard University · DP1 · FY2020 · AG
Immuno/Immuno-Gene Therapies for Thoracic Malignancies
$1,182,811Steven Mark Albelda · University Of Pennsylvania · P01 · FY2012 · CA
Immuno/Immunogene Therapies for Thoracic Malignancies
$1,182,811Steven Mark Albelda · University Of Pennsylvania · P01 · FY2010 · CA
Immuno/Immuno-Gene Therapies for Thoracic Malignancies
$1,182,811Steven Mark Albelda · University Of Pennsylvania · P01 · FY2016 · CA
Immuno/Immuno-Gene Therapies for Thoracic Malignancies
$1,182,811Steven Mark Albelda · University Of Pennsylvania · P01 · FY2015 · CA
PREQUEL Study In PRE-manifest HD of CoQ10/UbiquinonE Leading to Preventive Trials
$1,182,774Christopher A Ross · Johns Hopkins University · R01 · FY2008 · NS
Mayo Translational PKD Center (MTPC)
$1,182,745Vicente E Torres · Mayo Clinic Rochester · P30 · FY2010 · DK
Mayo Translational PKD Center (MTPC)
$1,182,744Vicente E Torres · Mayo Clinic Rochester · P30 · FY2011 · DK
An unbiased OMICs approach to identify mechanisms of Cocaine regulation of the HIV reservoir.
$1,182,718Rafick-Pierre Sekaly · Case Western Reserve University · R01 · FY2017 · DA
Mechanistic and translational studies of CBF leukemia
$1,182,715Paul Liu · National Human Genome Research Institute · ZIA · FY2013 · HG
Controlling Hematopoietic Lineage Commitment from ESC to Platelets
$1,182,659Beverly J Torok-Storb · Fred Hutchinson Cancer Research Center · U01 · FY2011 · HL
Research Project III - Vesicant-Induced Lung Injury
$1,182,647Debra Lynn Laskin · Rbhs-School Of Public Health · U54 · FY2017 · AR
Novel compounds for the treatment of systemic sclerosis-associated interstitial lung disease
$1,182,632Scott Scarneo · Eydis Bio, Inc. · R44 · FY2024 · HL
PROSTATE CANCER: TRANSITION TO ANDROGEN-INDEPENDENCE
$1,182,577University Of North Carolina Chapel Hill · P01 · FY2002 · CA
CREBRF and risk of pregnancy and postpartum dysglycemia in American Samoan womenÂ
$1,182,455Nicola Hawley · Yale University · R01 · FY2025 · DK